资讯出处:Researchers correct genetic mutation that causes IPEX, a life-threatening autoimmune syndrome
原始出处:Katelyn E. Masiuk, Jennifer Laborada, Maria Grazia Roncarolo, Roger P. Hollis, Donald B. Kohn. Lentiviral Gene Therapy in HSCs Restores Lineage-Specific Foxp3 Expression and Suppresses Autoimmunity in a Mouse Model of IPEX Syndrome. Cell Stem Cell, 2019; DOI: 10.1016/j.stem.2018.12.003